2nd Asia-Pacifiic Lysosomal Conference 2019

28th February 2017 - Pharma Company gives up on Pharmac

Sanofi Genzyme developed Myozyme, a complex biological treatment for Pompe disease, a lysosomal disease, over ten years ago. Since that time funded treatment of affected patients has spread to 76 countries. Over that decade, NZ's drug purchasing agency Pharmac has consistently refused to fund it, leaving the 10 patients here abandoned and facing relentless decline in their health and quality of life.

After substantial renewed efforts to negotiate with Pharmac, and with a recent recommendation from Pharmac's PTAC committee, released early February, that funding should be declined, the company has decided to provide the treatment free to four NZ patients. Read more here.